15th Workshop, Paris: “Compassionate Access to Rare Disease Therapies”

15th Workshop of the EURORDIS Round Table of Companies

“Compassionate Access to Rare Disease Therapies”


November 21th, 2011

Paris, France

15th ERTC Workshop

Six years after the inclusion of Compassionate Use (CU) in the European legislation (EC), and after our first ERTC Workshop on this topic, it was important to take stock of the progress made and discuss the difficulties encountered in its implementation.

Participants: 82


Concept Paper



For ERTC Members only, this document is password protected. If you want to become a member, find out more here or contact Anne-Mary Bodin, Operations Assistant.


The voice of rare disease patients in EuropeEURORDIS The international voice of people living with rare diseases, Rare Diseases International is a EURORDIS initiativeRare Disease International Bringing together patients, families and experts to share experiences in a moderated multilanguage forum, RareConnect is a EURORDIS initiative RareConnect The Rare Barometer Programme is a EURORDIS initiative that carries out surveys to transform rare disease patients' experiences into figures and facts that can be shared with decision-makers.Rare Barometer An international awareness raising campaign taking place on the last day of February each year, Rare Disease Day is a EURORDIS initiativeRare Disease Day Join the largest gathering of rare disease stakeholders across Europe, at the biennial European Conference on Rare Diseases and Orphan Products. ECRD is a EURORDIS initiativeEuropean Conference on Rare Diseases